Gangliosidoses, GM2

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Information
Disease name
Gangliosidoses, GM2
Disease ID
Description
Disease area statistics
[No Data.]
Chromosome band
[No Data.]
Annotation
Genes Mutation Description Source Links
NCT ID Status Phase Summary Start date Completion date
NCT01102686 Completed Phase 1/Phase 2 Pyrimethamine as a Treatment for Late-Onset GM2-gangliosidosis (Tay-Sachs and Sandhoff Disease) August 2009 November 2010
MeSH unique ID (MeSH (Medical Subject Headings))
D020143