Gangliosidoses, GM2
Information
- Disease name
- Gangliosidoses, GM2
- Disease ID
- Description
Disease area statistics
[No Data.]
Chromosome band
[No Data.]
Annotation
Genes | Mutation | Description | Source | Links |
---|
NCT ID | Status | Phase | Summary | Start date | Completion date |
---|---|---|---|---|---|
NCT01102686 | Completed | Phase 1/Phase 2 | Pyrimethamine as a Treatment for Late-Onset GM2-gangliosidosis (Tay-Sachs and Sandhoff Disease) | August 2009 | November 2010 |
- MeSH unique ID (MeSH (Medical Subject Headings))
- D020143